BioMarin’s (BMRN) Phase 3 Trial of BMN 401 for ENPP1 Deficiency Meets One Co-Primary Endpoint

3 days ago 4

Maham Fatima

Thu, May 21, 2026 astatine 8:29 AM CDT 1 min read

BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) is 1 of the best debased priced stocks to bargain for the adjacent 3 years. On May 18, BioMarin’s Phase 3 ENERGY 3 proceedings of BMN 401 for children with ENPP1 deficiency met lone 1 of its 2 co-primary endpoints. Treatment led to statistically important increases successful plasma inorganic pyrophosphate/PPi attraction done week 52 compared to accepted therapy.

However, the cause failed to amended Radiographic Global Impression of Change/RGI-C scores, a captious measurement of rickets severity. No affirmative trends were observed successful secondary endpoints similar maturation Z-scores oregon Rickets Severity Scores, though the attraction was well-tolerated with nary caller information signals.

BioMarin’s (BMRN) Phase 3 Trial of BMN 401 for ENPP1 Deficiency Meets One Co-Primary Endpoint

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Management expressed disappointment that the accrued PPi levels did not output objective benefits for the 27 pediatric participants. BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) is evaluating the information to find its adjacent steps and plans to contiguous elaborate results astatine an upcoming aesculapian meeting.

BioMarin Pharmaceutical Inc. (NASDAQ:BMRN) develops and commercializes therapies for superior and life-threatening aesculapian conditions and uncommon diseases. The company’s merchandise pipeline includes Valoctocogene roxaparvovec, Vosoritide, and BMN 307.

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